Gene-replacement therapy in neurodevelopmental disorders: progress and challenges - JCI

Retrieved on: 2025-02-03 17:16:21

Tags for this article:

Neurotransmitter transporters

Gaba

Signal transduction

Solute carrier family

GABA transporter type 1

Transmembrane receptors

Spinal muscular atrophy

Neurotransmitter sodium symporter

Click the tags to see associated articles and topics

Gene-replacement therapy in neurodevelopmental disorders: progress and challenges - JCI. View article details on hiswai:

Excerpt

( B ) Evaluation of GAT1 restoration to Slc6a1 knockout mice using AAV vector-based gene therapy involved different injection sites and developmental ...

Article found on: www.jci.org

View Original Article