Gene Therapy Improves Motor Function in Spinal Muscular Atrophy Type 2 - eMPR.com

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Gene Therapy Improves Motor Function in Spinal Muscular Atrophy Type 2 - eMPR.com. View article details on hiswai:

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Topline data were announced from a phase 3 trial evaluating intrathecal onasemnogene abeparvovec (OAV101 IT), an investigational gene therapy, ...

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