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Intellia's CRISPR Therapy Shows 90%+ Disease Protein Reduction in Key Clinical Trial

Retrieved on: 2024-11-17 02:14:16

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Summary

The article discusses Intellia Therapeutics' positive Phase 1 trial results for a CRISPR-based gene editing therapy, nex-z, in treating ATTR amyloidosis. The therapy reduces transthyretin protein, showing potential to stabilize or improve conditions linked to protein misfolding, like cardiomyopathy and polyneuropathy, relating to the key concept of 'protein folding.' Tags highlight related diseases and technologies.

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