Lifeline for Wolman disease kids as NICE backs Alexion drug - Pharmaphorum

Retrieved on: 2023-11-28 04:48:31

Tags for this article:

Lipid storage disorders

Acid lipase disease

Lysosomal acid lipase deficiency

Kanuma

Sebelipase alfa

Wolman

National Health Service

National Institute for Health and Care Excellence

NHS Scotland

Organ transplantation

Synageva

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Lifeline for Wolman disease kids as NICE backs Alexion drug - Pharmaphorum. View article details on HISWAI: https://pharmaphorum.com/news/lifeline-wolman-disease-kids-nice-backs-alexion-drug

Excerpt

... AstraZeneca's Alexion unit – after the company reached a commercial deal with NHS England. There are currently less than a dozen children in the ...

Article found on: pharmaphorum.com

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