Opus Genetics Receives Rare Pediatric Disease Designation from the U.S. FDA for Ocular ...

Retrieved on: 2024-08-20 18:06:53

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Gene delivery

Medical genetics

Molecular biology

Rare diseases

Blindness

Foundation Fighting Blindness

Gene therapy

Leber congenital amaurosis

Gene therapy of the human retina

Priority review

Retina

Voretigene neparvovec

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Opus Genetics Receives Rare Pediatric Disease Designation from the U.S. FDA for Ocular .... View article details on hiswai:

Excerpt

... gene therapy OPGx-LCA5 to treat patients with the inherited retinal disease LCA5. ... Gene Therapies Break Through Against Genetic Hearing Loss ...

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